The U.S. Food and Drug Administration has approved expanded use of Amgen's drug, Uplizna, to help reduce the risk of flares ...

Most cases of nocardiosis start out as lung infections, in which pus-filled cavities, or abscesses containing the bacteria, ...

AI helped Thomas Wagner understand Alexander disease, find connection with other conditions and discover researchers who ...

The drug fosdenopterin/rcPMP considerably improves the chances of survival and developmental progress in infants with ...

Khartik Uppalapati, 16, of Fairfax County, Virginia, has co-founded an advocacy group aimed at helping young people, like ...

The FDA has granted orphan drug designation to rilzabrutinib for IgG4-related disease and warm autoimmune hemolytic anemia, ...

After a devastating family loss, Chicago Med character Caitlin Lenox remains haunted by GSS, a rare, genetic prion disease.

At only two days old, Sophie was losing too much weight, and too quickly. Further genetic testing would show that Sophie has ...

My son is 8 and doctors are saving his life but worries we can go extinct from stupidity. He’s not wrong. News Editor Allison ...

After thinking he just had a stubborn sinus infection that wouldn't go away, Brian McNamara was told he had an ultra-rare ...

Sanofi SNY announced that the FDA has granted orphan drug designation to its investigational BTK inhibitor, rilzabrutinib, ...

A Michigan resident has died from rabies following a kidney transplant at a hospital in Ohio. Investigations show that the ...