In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...
The arc of biotechnology is one of breakthroughs and struggles, writes Tim Hunt, CEO of the Alliance for Regenerative ...
Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...
Scientists at the Allen Institute have made a major breakthrough in research for people living with Dravet Syndrome, which is ...
Gene therapy pioneer Jim Wilson and researcher Kiran Musunuru are using contrasting approaches to overcome “irrational ...
Genetic engineering in non-human primates has long been limited by the need for virus-based gene delivery methods. Recently, ...
By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without side effects.
To Novartis, fresh late-stage data support the idea that its intrathecal drug, which has the same active ingredient as ...
Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...
A research team affiliated with the Nano Optics Group within the Department of Physics at UNIST has announced the successful ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback