Worley was part of a team that showed how the loss of one of the two proteins used in the test disrupts synapses and leads to ...

Scientists at Rady Children's Institute for Genomic Medicine, and the Department of Neurosciences and Pediatrics at the University of California, San Diego, have made a significant breakthrough in ...

Scientists at Rady Children's Institute for Genomic Medicine, and the Department of Neurosciences and Pediatrics at the ...

Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 ...